Bilirakis and Matsui File Legislation to Improve Drug Development Process for Rare Disease Patients
November 13, 2024
November 13, 2024
WASHINGTON, Nov. 13 -- Rep. Gus M. Bilirakis, R-Florida, issued the following news release:
Representatives Gus Bilirakis (R-FL) and Doris Matsui (D-CA) have filed the Scientific External Process for Educated Review of Therapeutics (EXPERT) Act. This bill requires the FDA to establish externally-led science-focused drug development meetings targeting rare diseases. Over 90% of rare diseases have no FDA-approved treatment. One driver is the difficulty for overworked FDA staff to delv . . .
Representatives Gus Bilirakis (R-FL) and Doris Matsui (D-CA) have filed the Scientific External Process for Educated Review of Therapeutics (EXPERT) Act. This bill requires the FDA to establish externally-led science-focused drug development meetings targeting rare diseases. Over 90% of rare diseases have no FDA-approved treatment. One driver is the difficulty for overworked FDA staff to delv . . .