UT-Southwestern Medical Center: Gene Therapy Offers Hope for Giant Axonal Neuropathy Patients
March 28, 2024
March 28, 2024
DALLAS, Texas, March 28 (TNSres) -- The University of Texas Southwestern Medical Center issued the following news release:
A gene therapy developed by researchers at UT Southwestern Medical Center for a rare disease called giant axonal neuropathy (GAN) was well tolerated in pediatric patients and showed clear benefits, a new study reports. Findings from the phase one clinical trial, published in the New England Journal of Medicine, could offer hope for patients with this rare condit . . .
A gene therapy developed by researchers at UT Southwestern Medical Center for a rare disease called giant axonal neuropathy (GAN) was well tolerated in pediatric patients and showed clear benefits, a new study reports. Findings from the phase one clinical trial, published in the New England Journal of Medicine, could offer hope for patients with this rare condit . . .